Pluto Bioinformatics
GSE112250: Promoter or enhancer activation by CRISPRa rescues haploinsufficiency caused obesity
Bulk RNA sequencing
Our results show that CRISPRa can be developed as a gene regulation therapy (GRT) to treat altered gene dosage diseases. SOURCE: Walter Eckalbar (walter.eckalbar@gmail.com) - University of California, San Francisco